Publication
The present invention is directed to new compositions uses thereof and related methods for the treatment of X- linked adrenoleukodystrophy.
Mats Julius Stensrud, Aaron Leor Sarvet
Christof Holliger, Aline Sondra Adler, Laetitia Janine Andrée Cardona, Jaspreet Singh Saini, Pilar Natalia Rodilla Ramírez, Ruizhe Pei