Early detection of white matter lesions in childhood-onset cerebral adrenoleukodystrophy (ALD) is important as hematopoietic cell transplantation (HCT), currently the only effective treatment, is beneficial only if performed early in the disease course.
Christophe Ballif, Jonas Geissbühler, Matthieu Despeisse, Mathieu Gérard Boccard, Jean Cattin